“As yet, there is no complete cure for SMA. However, the discovery of the genetic cause of SMA has led to the development of several treatment options that affect the genes involved in SMA — a gene replacement therapy called Zolgensma, and two drugs, called nusinersen (Spinraza) and risdiplam (Evyrsdi).”

Boston Children’s Hospital (https://www.childrenshospital.org/conditions/spinal-muscular-atrophy-sma)